Perspectives on Enquiry & Evidence
Cytel's blog featuring the latest industry insights.
March 11, 2024
In 2023, rare diseases accounted for 30% of product pipeline under development, about half of which comprising...
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February 26, 2024
Sample Size Re-Estimation for Rare Disease Clinical Trials
Written by Boaz N. Adler, MPA, Director, Global Product Engagement, and Valeria Mazzanti, MPH, Associate Director,...
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February 13, 2024
Strategies to Overcome Limited Patient Population Challenges in Rare Disease Studies
Written by Boaz N. Adler, MPA, Director, Global Product Engagement, and Valeria Mazzanti, MPH, Associate Director,...
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September 7, 2018
Opportunities of FDA’s Innovative Trial Design Pilot Meeting Program
On August 29th 2018, the FDA announced (1) that it would be establishing a Complex Innovative Trial Design (CID) Pilot...
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September 29, 2016
Case studies:Learning from less-well understood adaptive designs
A paper "Best practices case studies for 'less well-understood' Adaptive designs", has been published by the DIA...
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September 9, 2016
Case Study:Seamless Phase 2/3 Design in Rare Disease
Challenge: Our client, an emerging biotechnology company, was preparing for the next stage of development for their...
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July 18, 2016
Adaptive Design in the limelight with NEJM article
In order for adaptive designs to reach their potential, it’s critical that knowledge is effectively dissemirnated...
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